Stem Cells For Personalized Regenerative Medicine: A Systems Approach

During the past ten years since the sequencing ofFollowing isolation of the stem cells, further
the human genome, personalized medicine whereprocessing can be performed.  Processing can be
therapeutics are developed for the individual from theminimal, and the "minimally processed" cells used for
person's genetic information has shown promise formedical procedures, or the stem cells can be
delivering more efficacy and fewer side-effects.processed in a number of ways such that the stem
However, despite many scientific gains in genomicscells now become classified as "biologics" requiring
during the past decade, human health, according toFDA approval for their use in patients. As an
Dr. Francis Collins and Dr. Craig Venter, leaders of theexample, stem cells can be processed in order to
genomic revolution, has only marginally benefitedcause the cells to differentiate. When stem cells
from the sequencing of the human genome (Nature,differentiate, the stem cell becomes modified into a
464, 649-650, 1 April 2010). The field ofmore mature cell and may transform into, for
pharmacogenomics is still in its early stages. Geneticexample, a cardiac cell. In this case, the differentiated
variations within individuals may exist in the millions,cardiac cell can now be implanted into a patient for
and identifying the variations may require manytreatment of heart conditions.  Because the patient's
years, or decades. In addition, how  an individualstem cell was differentiated into a heart cell and then
responds to a medication will probably not beimplanted into the patient, instead of implanting the
determined by just one gene but rather by manystem cell itself, FDA will consider the differentiated
genes interacting with one another. Biology does notheart cell a biologic and require approval.
act in a reductionist manner, rather biologicalWhile processing the stem cells into FDA approved
phenomenon, including therapeutics, act as a system.biologics may prove useful for many indications, many
Examining this complicated genetic map is expensivestudies have demonstrated the remarkable efficacy
and time-consuming. As a result, pharmacogenomicsof using minimally processed stem cells in medical
as a routine part of medicine is likely decades away.procedures. Although many challenges face the new
Unlike the relatively slow progress being made in thefield of stem cell therapeutics, one of the key
development of drugs through a process offeatures of stem cells learned during the 1990s is
understanding an individual's genome, and thentheir ability to heal tissue by releasing a multitude of
developing a targeted drug based on the individual'smolecules into the damaged tissue. The release of
genetic information, known as pharmacogenomicsthese molecules into the damaged tissue is an
(PGx),  this means for developing drugs forimportant, if not primary, means for many indications
personalized medicine has yet to realize thein the stem cell's capacity to promote healing. Thus,
therapeutic potential that autologous stem cellthe stem cell can be considered a mobile factory for
procedures have realized.the production of the multitude of molecules, the
Personalized regenerative medicine for manymultitude of healing molecules (Singec, I. 2008 Stem
indications can now be realized through autologousCells, 1: 313-328).
stem cell therapeutics. Harvesting potent stem cells isUsing the stem cells to generate a multitude of
easily accomplished by lipo-aspirating fat from themolecules is a "systems approach" to developing a
patient, and then separating mesenchymal stem cellstherapeutic. As discussed in the aforementioned
from the adipose tissue. The mesenchymal stem cellssection, biological processes do not act alone; single
can be further processed for a number ofmolecules are a component of a larger process. If
procedures and have been shown to be very potentone studies the healing process of wounded skin for
therapeutic agents for many indications, includingexample, there is a cascade of events involved
cardiac, CNS, immune system, joint, and plasticwhere many molecules act within a system to
reconstructive procedures. Further, becausepromote healing of the wound. Using just one of the
mesenchymal stem cells avoid allogenic rejectionmolecules to promote healing of the wound may
(Ryan, J. Inflammation 2005, 2:8), these cells have thehave some utility, but the efficacy will not compare
potential of being used more widely, such as recentto using the full complement of molecules. In a 2010
treatments at several children's hospitals in the US,study that included Dr. Collins as an author, a scan of
where allogenic stem cells have been used tohuman DNA revealed that 95 genes affect blood
enhance the immune system in children.cholesterol. Thus, here again, a system of 95 genes,
Let's consider the procedure in more detail. A numberand likely 95 or more molecules, is affecting
of sources for potent stem cells exist in the body,cholesterol levels. Likewise, when stem cells are
including adipose (fat) tissue. Fat provides a reservoirinjected into the body where they release their
for mesenchymal stem cells, where the stem cellsmultitude of molecules, a systems approach to
reside in a dormant state until they are recruited forhealing, and therefore an approach with high efficacy,
purposes of healing. Mesenchymal stem cells are ais being administered. Further, in the case of
type of stem cell that has been shown to promoteautologous procedures, one is receiving the multitude
healing of many types of tissue. Using a needle andof stem cell released molecules (termed the SRM at
syringe, a small amount of fat is extracted from theBioRegenerative Sciences, Inc.) from one's own body;
patient's thigh, for example. This can be a simplea personalized medical procedure where the
out-patient procedure. Fat can also be, of course,molecules are genetically matched to the
extracted from the patient during more extensivepatient. This systems approach in the healing
cosmetic liposuction procedures. Once a small amountprocess mediated by stem cells renders the
of fat has been extracted, the fat is processed inadministration of stem cells to the patient as the
the lab using a centrifuge procedure to separate theforemost means for delivering "personalized
stem cells.regenerative medicine" to the patient.